A Phase 2 Randomized, Double Blind Placebo-Controlled, Parallel Group Study to Evaluate the Dose and Pharmacodynamic Efficacy of Sialic Acid Extended

Project Summary

The effect of this medication on strength, walking ability and activities of daily living is being evaluated for this fairly rare progressive adult neuromuscular disorder. A label aspect has begun (beginning 6/2013) as patients complete the initial study they are invited to continue in this new phase.

Timescale: 06/01/2012 - 08/30/2021
Current status: Project live


Primary Investigator: Eileen Fowler